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The first clinical gene therapy was given in 1990 to a 4 years old girl with enzyme deficiency of

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The first clinical gene therapy was given in 1990 to a 4 years old girl with enzyme deficiency of

(a) Adenosine deaminase (ADA)

(b) Tyrosine oxidase

(c) Monoamine oxidase

(d) Glutamate dehydrogenase

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(a) Adenosine deaminase (ADA)

Explanation:

Gene therapy is an experimental technique that uses genes to treat or prevent disease. The first clinical gene therapy was given for treating adenosine deaminase deficiency. A four-year old girl became the first gene therapy patient on September 14, 1990 at the NIH Clinical Center. Adenosine deaminase deficiency, also called ADA deficiency or ADA-SCID is an autosomal recessive metabolic disorder that causes immunodeficiency. ADA deficiency is due to a lack of the enzyme adenosine deaminase.

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